Stem cell and gene therapy13 Jan 2023 13:39
Sometime before the end of March, a person with the inherited blood disease beta thalassemia will receive an infusion containing hundreds of millions of their own stem cells. These cells will have just completed a round-trip journey to a drug manufacturing facility, where they'll be equipped with a modified gene capable of fixing the patient's condition.
The expected infusion will be the first commercial use of a gene therapy approved by the Food and Drug Administration in August.
This is off course hugely relevant for Avacta and the value of it’s holding in Affyxel and events last year:
AffyXell, Avacta’s joint venture with Daewoong Pharmaceutical, expands its manufacturing partnership with GenScript ProBio for cell therapies
GenScript ProBio agrees to take an equity stake in AffyXell as a strategic investor at next funding round