RE: Article22 Feb 2016 08:08
As I was posting a month or two back... these orphan drugs are very big business although niche.
Uncanny that the founder of Shire, a multi billion £ pharma company that specialises in Orphan drugs will now be chairing this new company...that by the way is currently valued just at cash! seriously excited.
Article from FT that I posted a month or two back well worth a read:
http://www.ft.com/cms/s/0/594cf986-271c-11e5-bd83-71cb60e8f08c.html
"Orphan drugs might target small groups of patients, but they are increasingly big business.
Pharmaceutical companies, from tiny biotech start-ups to Shire, the London-listed group with a market capitalisation of more than £30bn, are focusing on drugs for orphan diseases, lured by regulatory incentives and a low-volume, high-margin business model.
Ever since the introduction of the US Orphan Drug Act 32 years ago, developing medicines for rare disease has become the so-called “Goldilocks option” for some pharma companies.
Groups selling orphan drugs are granted seven years of market exclusivity (against five years for most medicines), along with generous tax credits. Because they target diseases that do not already have treatments, they also tend to benefit from other regulatory initiatives designed to get drugs to market more quickly.
Once approved, the drugs often have a ready-made audience: many patients with rare diseases are well organised in advocacy groups, have been waiting for years for a treatment, and are primed to request the medicine from their doctors once it is available.
Global sales of orphan drugs are expected to jump as more companies enter this field, rising by 11 per cent each year to reach $176bn in 2020, according to EvaluatePharma, the research group.
Investors have taken notice. In the past year, the value of US biotech companies focused on rare diseases has risen by about 56 per cent, according to the Orphan Disease Index, assembled by JMP Securities, a San Francisco investment bank.
That performance was even better than the broader Nasdaq biotech index, which is up by roughly 37 per cent over the same period, and smashed the S&P 500 index, which is 5 per cent higher."
Have a good day folks.